A Long-Term Follow-Up Study in Subjects With Severe Hemophilia A Who Received BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in a Prior BioMarin Clinical Trial
Latest Information Update: 29 Apr 2024
At a glance
- Drugs Valoctocogene-roxaparvovec (Primary)
- Indications Haemophilia A
- Focus Adverse reactions
- Acronyms GENEr8-LTE
- Sponsors BioMarin Pharmaceutical
- 17 Mar 2023 New trial record