Post-trial Access Program: Idursulfase-IT (HGT-2310) in Conjunction With Intravenous Elaprase® in Pediatric and Adult Patients With Hunter Syndrome and Cognitive Impairment
Latest Information Update: 10 Apr 2024
At a glance
- Drugs Idursulfase (Primary) ; Idursulfase (Primary)
- Indications Cognition disorders; Mucopolysaccharidosis II
- Focus Expanded access; Therapeutic Use
- Sponsors Takeda
Most Recent Events
- 07 Apr 2023 New trial record