Trial Profile

An Open-label, Phase 2 Trial to Evaluate the Efficacy and Safety of a Single Intravenous Administration of GNT0003 (an Adeno-associated Viral (AAV) Vector Expressing the UGT1A1 Transgene) Following Imlifidase Pre-treatment in Adult Participants With Severe Crigler-Najjar Syndrome (CNS) Requiring Daily Phototherapy and Presenting Pre-existing Anti-AAV8 Antibodies

Status: Recruiting

Phase of Trial: Phase II

Latest Information Update: 06 Dec 2024

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At a glance

28 Nov 2024 Status changed from not yet recruiting to recruiting.
29 Jul 2024 Status changed to not yet recruiting.
02 Feb 2024 According to Hansa Biopharma AB media release, initiation of clinical study with imlifidase prior to GNT-0003 will be in 2024.

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