Trial Profile

A Phase IV Open-Label Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

Status: Recruiting

Phase of Trial: Phase IV

Latest Information Update: 19 Mar 2025

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At a glance

06 Aug 2024 Planned initiation date (estimated date of first participant enrollment) changed from 31 May 2024 to 16 Aug 2024.
29 Mar 2024 Planned initiation date (estimated date of first participant enrollment) changed from 20 Apr 2024 to 31 May 2024.
12 Mar 2024 Planned initiation date (estimated date of first participant enrollment) changed from 12 Mar 2024 to 20 Apr 2024.

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