A Phase 1/2, Open-label, Multi-national, Multiple-cohort, Dose-escalation Study to Evaluate the Safety, Tolerability, and Efficacy of HG004 Gene Therapy in Subjects with RPE65-associated Leber Congenital Amaurosis Type 2 (LCA2)
Latest Information Update: 27 Sep 2024
At a glance
- Drugs HG-004 (Primary)
- Indications Leber congenital amaurosis
- Focus Adverse reactions
- Acronyms STAR
- Sponsors HuidaGene Therapeutics
Most Recent Events
- 01 Nov 2023 According to a HuidaGene Therapeutics Media Release, first patient has been dosed in this trial.
- 26 Oct 2023 Planned initiation date changed (estimated date for recruitment of the first subject) to 1 Oct 2023.
- 20 Jun 2023 New trial record