Trial Profile

An observational study of Children With Spinal Muscular Atrophy Treated With Nusinersen/Risdiplam

Status: Completed

Phase of Trial: Phase IV

Latest Information Update: 12 Jul 2023

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At a glance

Drugs Risdiplam (Primary)
Indications Spinal muscular atrophy
Focus Therapeutic Use

Most Recent Events

12 Jul 2023 New trial record
24 May 2023 Results presented at the 119th International Conference of the American Thoracic Society

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