Early Access Program (EAP) for Danicopan as Add-on Treatment to SOLIRIS® or ULTOMIRIS® in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have Clinically Significant Extravascular Hemolysis (csEVH)
Latest Information Update: 19 Apr 2025
At a glance
- Drugs Danicopan (Primary) ; Eculizumab (Primary) ; Ravulizumab (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Expanded access; Therapeutic Use
- Sponsors Alexion AstraZeneca Rare Disease
Most Recent Events
- 14 Aug 2023 New trial record