A phase II, multicenter, open label study to evaluate the efficacy and safety of Luspatercept (ACE-536) in adult patients with Congenital Dyserythropoietic Anemia type Il (CDA ll). Studio di Fase 2, aperto, multicentrico per determinare l'efficacia e la sicurezza di Luspatercept (ACE-536) in soggetti adulti affetti da Anemia Diseritropoietica Congenita tipo II (CDA II).
Latest Information Update: 25 Aug 2023
At a glance
- Drugs Luspatercept (Primary)
- Indications Congenital-dyserythropoietic-anemia
- Focus Therapeutic Use
- 25 Aug 2023 New trial record