An Expanded Access Program of Pozelimab and Cemdisiran Combination Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria
Latest Information Update: 07 Nov 2025
At a glance
- Drugs Cemdisiran (Primary) ; Pozelimab (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Expanded access; Therapeutic Use
- Sponsors Regeneron Pharmaceuticals
Most Recent Events
- 20 Oct 2025 Status changed from recruiting to completed.
- 11 Sep 2023 New trial record