MAP THE SMA: a Machine-learning Based Algorithm to Predict THErapeutic Response in Spinal Muscular Atrophy
Latest Information Update: 18 Sep 2023
At a glance
- Drugs Nusinersen (Primary) ; Onasemnogene-abeparvovec (Primary) ; Risdiplam (Primary)
- Indications Spinal muscular atrophy
- Focus Biomarker; Therapeutic Use
- Acronyms MAP THE SMA; MAP_THE_SMA-01
- 18 Sep 2023 New trial record