A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of Vosoritide in Children with Hypochondroplasia
Latest Information Update: 08 Jun 2025
At a glance
- Drugs Vosoritide (Primary)
- Indications Hypochondroplasia
- Focus Registrational; Therapeutic Use
- Sponsors BioMarin Pharmaceutical
Most Recent Events
- 12 May 2025 According to a BioMarin Pharmaceutical media release, BioMarin completed enrollment in its pivotal Phase 3 study with VOXZOGO in hypochondroplasia in April, and the company is on track to share topline data in 2026, with potential launch in 2027.
- 12 May 2025 According to a BioMarin Pharmaceutical media release, status changed from recruiting to active, no longer recruiting.
- 19 Feb 2025 According to a BioMarin Pharmaceutical media release, this study remains on track to launch in 2027.