A Phase 2a, Randomised, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy, Safety, and Tolerability of NMD670 Over 21 Days in Ambulatory Adult Patients With Type 1 and Type 2 Charcot-Marie-Tooth Disease
Latest Information Update: 14 Jul 2026
At a glance
- Drugs Ignaseclant (Primary)
- Indications Charcot-Marie-Tooth disease
- Focus Therapeutic Use
- Acronyms ESTABLISH1; SYNAPSE-CMT
Most Recent Events
- 17 Jun 2026 According to a NMD Pharma media release, data from this study has been presented in a late-breaking oral presentation at the 2026 Peripheral Neuroscience Association (PNS) Annual Meeting held in Maastricht, The Netherlands from June 13-16, 2026.
- 17 Jun 2026 Results presented in a NMD Pharma Media Release.
- 10 Mar 2026 According to a NMD Pharma media release, data from this study were presented at the 2026 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference.