A Phase 2a, Randomised, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy, Safety, and Tolerability of NMD670 Over 21 Days in Ambulatory Adult Patients With Type 1 and Type 2 Charcot-Marie-Tooth Disease
Latest Information Update: 18 Mar 2026
At a glance
- Drugs Ignaseclant (Primary)
- Indications Charcot-Marie-Tooth disease
- Focus Therapeutic Use
- Acronyms ESTABLISH1; SYNAPSE-CMT
Most Recent Events
- 10 Mar 2026 According to a NMD Pharma media release, data from this study were presented at the 2026 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference.
- 10 Mar 2026 Results presented in the NMD Pharma Media Release.
- 12 Feb 2026 According to a NMD Pharma media release, data from this study will be presented at the 2026 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference being held in Orlando, Florida from March 8-11, 2026.