Trial Profile

A Phase 1/2, Randomized, Double-blind, Placebo-controlled Single- and Multiple-dose Escalation Study Evaluating the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of VX-670 in Adult Subjects With Myotonic Dystrophy Type 1

Status: Recruiting

Phase of Trial: Phase I/II

Latest Information Update: 01 May 2025

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At a glance

24 Apr 2025 Planned End Date changed from 1 Dec 2026 to 31 Dec 2026.
24 Apr 2025 Planned primary completion date changed from 1 Dec 2026 to 31 Dec 2026.
12 Jan 2025 According to Vertex Pharmaceuticals media release, the company initiated the MAD portion of the Phase 1/2 study, which will assess both safety and efficacy.

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