Study of mRNA 3705 in Methylmalonic acidaemia patients
Latest Information Update: 12 Jun 2026
At a glance
- Drugs MRNA-3705 (Primary)
- Indications Methylmalonic acidaemia
- Focus Registrational; Therapeutic Use
Most Recent Events
- 01 May 2026 According to a Moderna Therapeutics media release,The Company is deferring its decision on a pivotal trial for mRNA-3705 until PA registrational data readout.
- 20 Nov 2025 According to a Moderna Therapeutics media release, study expected to begin in 2026.
- 01 May 2025 According to a Moderna Therapeutics media release, The Company expects to start a registrational study in 2025.