A Prospective, Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in Hereditary Tyrosinemia Type 1 (HT-1) Patients in Routine Clinical Care in China
Latest Information Update: 04 Apr 2025
At a glance
- Drugs Nitisinone (Primary)
- Indications Tyrosinaemia type I
- Focus Adverse reactions
- Sponsors Swedish Orphan Biovitrum
Most Recent Events
- 31 Jan 2024 New trial record