Trial Profile

First in Human Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Multiple Ascending Doses of Intrathecally Administered ALN-SOD in Participants With Amyotrophic Lateral Sclerosis and SOD1 Mutations

Status: Recruiting

Phase of Trial: Phase I

Latest Information Update: 05 Jun 2025

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At a glance

19 Sep 2024 Status changed from not yet recruiting to recruiting.
15 Aug 2024 Planned End Date changed from 28 Apr 2029 to 26 Apr 2029.
15 Aug 2024 Planned primary completion date changed from 28 Apr 2029 to 26 Apr 2029.

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