Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I) Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of Autologous Hematopoietic Stem Cells Transduced With a Lentiviral Vector Encoding the ITGB2 Gene
Latest Information Update: 07 Mar 2024
At a glance
- Drugs Marnetegragene autotemcel (Primary)
- Indications Leukocyte-Adhesion Deficiency Syndrome
- Focus Therapeutic Use
- Sponsors Rocket Pharmaceuticals
Most Recent Events
- 07 Mar 2024 New trial record