A Phase 3b Open-Label Study of Long-Term Neurocognitive Outcomes in Children With Phenylketonuria Treated With Sepiapterin
Latest Information Update: 30 Sep 2024
At a glance
- Drugs Sepiapterin (Primary)
- Indications Phenylketonuria
- Focus Registrational; Therapeutic Use
- Acronyms EPIPHENY
- Sponsors PTC Therapeutics
Most Recent Events
- 10 May 2024 Status changed from not yet recruiting to recruiting.
- 12 Mar 2024 New trial record