A Multi-Center, Prospective, Longitudinal, Study Evaluating Immunologic, Inflammatory, and Laboratory Parameters Associated With Long-Term Palynziq® (Pegvaliase) Treatment in Subjects With Phenylketonuria (PKU) in the United States
Latest Information Update: 28 Aug 2024
At a glance
- Drugs Pegvaliase (Primary)
- Indications Phenylketonuria
- Focus Therapeutic Use
- Acronyms PALisade
- Sponsors BioMarin Pharmaceutical
Most Recent Events
- 14 Mar 2024 New trial record