Trial Profile

An Open, Dose-escalation, Phase 1b Clinical Trial to Evaluate the Safety and Efficacy of EN001 in Patients With Charcot-Marie-Tooth Disease Type 1A (CMT1A)

Status: Active, no longer recruiting

Phase of Trial: Phase I

Latest Information Update: 29 Aug 2025

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At a glance

Drugs EN 001 (Primary)
Indications Charcot-Marie-Tooth disease
Focus Adverse reactions
Sponsors ENCell

Most Recent Events

12 Aug 2025 Planned End Date changed from 1 Oct 2024 to 1 Oct 2025.
12 Aug 2025 Planned primary completion date changed from 1 Oct 2024 to 1 Oct 2025.
12 Aug 2025 Status changed from recruiting to active, no longer recruiting.

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