Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia
Latest Information Update: 22 Oct 2024
At a glance
- Drugs LX 2006 (Primary) ; Prednisone (Primary)
- Indications Cardiomyopathies; Friedreich's ataxia
- Focus Adverse reactions
- 17 Oct 2024 Planned number of patients changed from 10 to 25.
- 15 Jul 2024 According to a LEXEO Therapeutics Media Release, Weill Cornell investigator-initiated trial is currently enrolling in Cohort 2.
- 09 May 2024 According to Lexeo Therapeutics, Inc. media release, the company has completed in-license agreement with Cornell University for intellectual property rights, including current and future clinical data from an ongoing investigator-initiated trial of AAVrh.10hFXN (LX2006) to support regulatory discussions.