Trial Profile

A Phase 1/2a, Open-Label, Multi-Center, Dose-Escalation Trial to Assess Safety, Tolerability, and Efficacy of a Single Dose of CAP-002 Gene Therapy Administered to Pediatric Patients With Syntaxin-Binding Protein 1 (STXBP1) Encephalopathy

Status: Suspended

Phase of Trial: Phase I/II

Latest Information Update: 14 Oct 2025

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At a glance

01 Oct 2025 Status changed from recruiting to suspended because stopping rule was met as per the protocol. Before resuming the enrollment, comprehensive review is needed.
08 Jul 2025 Status changed from not yet recruiting to recruiting.
29 May 2025 According to Capsida Biotherapeutics media release, the company is initiating study start-up activities for this trial.

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