Trial Profile

A phase 3 study of NTLA-2001 for the treatment of hereditary ATTR amyloidosis with polyneuropathy,

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 15 May 2024

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At a glance

Drugs Nexiguran-ziclumeran (Primary)
Indications Familial amyloidosis
Focus Therapeutic Use

Most Recent Events

15 May 2024 New trial record
10 May 2024 According to Intellia Therapeutics media release, Aligned with FDA on design for a new Phase 3 trial of NTLA-2001 for the treatment of hereditary ATTR amyloidosis with polyneuropathy, subject to review of IND application; expect to initiate the study by year-end

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