A Multi-center, Open Label, Single-arm, Dose Ascending Clinical Trial for Evaluation of Safety and Efficacy of Gene Therapy Drug GC101 in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients
Latest Information Update: 27 Sep 2024
At a glance
- Drugs GC 101 (Primary)
- Indications Spinal muscular atrophy
- Focus Adverse reactions; Therapeutic Use
- Sponsors GeneCradle Therapeutics
- 22 May 2024 New trial record