A PHASE 2, TWO-PART, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, MULTICENTER STUDY TO EVALUATE THE EFFICACY, SAFETY, AND TOLERABILITY OF SUBCUTANEOUSLY ADMINISTERED REGN7999 (AN INHIBITOR OF TMPRSS6) IN PARTICIPANTS WITH IRON OVERLOAD DUE TO NON-TRANSFUSION DEPENDENT β-THALASSEMIA
Latest Information Update: 10 Mar 2025
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At a glance
- Drugs REGN-7999 (Primary)
- Indications Beta-thalassaemia
- Focus Adverse reactions; Therapeutic Use
- Acronyms FERVENT-1
- Sponsors Regeneron Pharmaceuticals
- 14 Oct 2024 Status changed from not yet recruiting to recruiting.
- 22 May 2024 New trial record