A compassionate use study of leriglitazone for treatment of progressive cerebral adrenoleukodystrophy (cALD) in adult male patients
Latest Information Update: 17 Jun 2024
At a glance
- Drugs Leriglitazone (Primary)
- Indications Adrenoleucodystrophy
- Focus Expanded access; Therapeutic Use
- 17 Jun 2024 New trial record
- 11 Jun 2024 According to a Minoryx Therapeutics Media Release, this compassionate-use study was led by Fanny Mochel, MD, Ph.D., professor at the Hospital Universitaire La Pitie-Salpetriere (Paris, France), as part of an early-access program through the French national drug agency (ANSM) that allows for the use of innovative treatments with favorable safety profiles under a Compassionate Access Authorization protocol (ATU).
- 11 Jun 2024 According to a Minoryx Therapeutics Media Release, resuls from this trial published in the peer-reviewed journal Brain.