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Pilot Study Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

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Trial Profile

Pilot Study Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

Status: Recruiting
Phase of Trial: Phase IV

Latest Information Update: 08 Sep 2025

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At a glance

Most Recent Events

  • 15 Aug 2025 Planned End Date changed from 1 Nov 2026 to 1 Mar 2027.
  • 15 Aug 2025 Planned primary completion date changed from 1 May 2026 to 1 Sep 2026.
  • 15 Aug 2025 Planned initiation date changed from 1 Aug 2025 to 1 Oct 2025.

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