A Phase 3 Open-Label Study of Safety, Pharmacokinetics, and Activity of Weekly Subcutaneous Pegzilarginase in Subjects <24 Months Old With Arginase 1 Deficiency
Latest Information Update: 05 Sep 2024
At a glance
- Drugs Pegzilarginase (Primary)
- Indications Hyperargininaemia
- Focus Therapeutic Use
- Sponsors Immedica
- 05 Sep 2024 New trial record