An Open-Label, Systemic Gene Delivery Study to Evaluate the Safety, Tolerability and Expression of Delandistrogene Moxeparvovec Following Plasmapheresis in Subjects With Duchenne Muscular Dystrophy and Pre-existing Antibodies to AAVrh74

Status: Not yet recruiting

Phase of Trial: Phase I

Latest Information Update: 01 Oct 2024

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At a glance

Drugs Delandistrogene moxeparvovec (Primary)
Indications Duchenne muscular dystrophy
Focus Pharmacodynamics; Therapeutic Use
Acronyms HORIZON
Sponsors Sarepta Therapeutics

Most Recent Events

01 Oct 2024 New trial record

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