Trial Profile

An open-label, single-arm, phase 1/2 first-in-human study to assess the safety and efficacy of autologous CD34+ cells transduced with a lentiviral vector encoding the human NCF1 gene (SGX-001) in paediatric and adult patients with chronic granulomatous disease caused by p47phox deficiency

Status: Not yet recruiting

Phase of Trial: Phase I/II

Latest Information Update: 11 Jun 2026

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At a glance

01 Jun 2026 Status changed from planning to not yet recruiting.
10 Oct 2024 New trial record
08 Oct 2024 According to Somagenetix AG media release, company looks forward to starting clinical application of SGX-001 during 2026.

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