An Open-label, Single-arm, Phase 1/2 First-in-human Study to Assess the Safety and Efficacy of Autologous CD34+ Cells Transduced With a Lentiviral Vector Encoding the Human NCF1 Gene (SGX-001) in Paediatric and Adult Patients With Chronic Granulomatous Disease Caused by p47phox Deficiency
Latest Information Update: 23 Sep 2026
At a glance
- Drugs SGX 001 (Primary)
- Indications Chronic granulomatous disease
- Focus Adverse reactions; First in man
- Sponsors Somagenetix
Most Recent Events
- 17 Sep 2026 Status changed from not yet recruiting to recruiting.
- 01 Jun 2026 Status changed from planning to not yet recruiting.
- 10 Oct 2024 New trial record