Trial Profile

GSDIa Disease Monitoring Program

Status: Recruiting

Phase of Trial: Phase IV

Latest Information Update: 25 Apr 2026

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At a glance

Drugs Pariglasgene brecaparvovec (Primary)
Indications Glycogen storage disease type I
Focus Adverse reactions
Sponsors Ultragenyx Pharmaceutical

Most Recent Events

25 Nov 2024 Status changed from not yet recruiting to recruiting.
15 Oct 2024 New trial record

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