A Phase 2, Randomized, Human Growth Hormone-Controlled, Multicenter, Basket Study of Vosoritide in Children With Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency, and Noonan Syndrome With an Inadequate Response to Human Growth Hormone. (CANOPY NS, TS, SHOX-D-2)
Latest Information Update: 21 May 2025
At a glance
- Drugs Vosoritide (Primary)
- Indications Noonan syndrome; Turner's syndrome
- Focus Therapeutic Use
- Acronyms CANOPY NS, TS, SHOX-D-2
- Sponsors BioMarin Pharmaceutical
Most Recent Events
- 12 May 2025 According to a BioMarin Pharmaceutical media release, the data from this study were presented as a poster presentation at the 2025 Joint Congress of the European Society for Paediatric Endocrinology (ESPE) and the European Society of Endocrinology (ESE) in Copenhagen, Denmark.
- 12 May 2025 According to a BioMarin Pharmaceutical media release, data from this study were presented at the Pediatric Endocrine Society Annual Meeting (PES).
- 16 Jan 2025 Status changed from not yet recruiting to recruiting.