A Long-term Follow-up Study Evaluating the Safety and Efficacy of Subjects With β-thalassemia Treated With Base-edited Autologous Hematopoietic Stem Cell (CS-101) Transplantation
Latest Information Update: 19 Feb 2025
At a glance
- Drugs CS 101 (Primary)
 - Indications Beta-thalassaemia
 - Focus Adverse reactions; Therapeutic Use
 - Sponsors CorrectSequence Therapeutics
 
Most Recent Events
- 19 Nov 2024 New trial record