A Phase 1/2 Open-label Intrathecal Administration of MELPIDA to Determine Its Safety and Efficacy for Patients with Spastic Paraplegia Type 50 (SPG50) Caused by Mutation in the AP4M1 Gene
Latest Information Update: 26 Nov 2024
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At a glance
- Drugs Gene therapies
- Indications Paraplegia
- Focus Adverse reactions
- Acronyms hAP4M1opt
- Sponsors Elpida Therapeutics
- 26 Nov 2024 New trial record