A Phase 1/2 Open-label Intrathecal Administration of MELPIDA to Determine Its Safety and Efficacy for Patients with Spastic Paraplegia Type 50 (SPG50) Caused by Mutation in the AP4M1 Gene
Latest Information Update: 17 Jan 2025
At a glance
- Drugs Melpida-Elpida Therapeutics (Primary)
- Indications Paraplegia
- Focus Adverse reactions
- Acronyms hAP4M1opt
- Sponsors Elpida Therapeutics
Most Recent Events
- 26 Nov 2024 New trial record