An Open Label, Single Arm, Dose Escalation Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of GCB-002 in the Treatment of Female Subjects with MECP2 Gene Mutation in Patients with Rett Syndrome
Latest Information Update: 14 Mar 2025
At a glance
- Drugs GCB 002 (Primary)
- Indications Rett syndrome
- Focus Adverse reactions; Therapeutic Use
- Acronyms GITFPWRS
- Sponsors Genecombio
Most Recent Events
- 07 Mar 2025 Status changed from not yet recruiting to recruiting.
- 25 Dec 2024 New trial record