An Off-Label Single Arm Clinical Study to Evaluate the Efficacy and Safety of Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency
Latest Information Update: 11 Aug 2025
At a glance
- Drugs Deoxycytidine/deoxythymidine (Primary)
- Indications Mitochondrial disorders
- Focus Therapeutic Use
Most Recent Events
- 28 Jul 2025 Planned number of patients changed from 5 to 15.
- 07 Jan 2025 New trial record
- 06 Jan 2025 Status changed from not yet recruiting to recruiting.