Trial Profile

A Phase 2 Double-Blinded, Randomized, Placebo-Controlled Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Status: Recruiting

Phase of Trial: Phase II

Latest Information Update: 22 Dec 2025

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At a glance

17 Dec 2025 Status changed from planning to recruiting.
31 Jul 2025 According to an argenx media release, study on track to start by end of year
17 Jan 2025 New trial record

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