Allogeneic Hematopoietic Stem Cell Transplant for Patients With High Risk Hemoglobinopathies and Other Red Cell Transfusion Dependent Disorders
Latest Information Update: 18 Mar 2025
At a glance
- Drugs Alemtuzumab (Primary) ; Antithymocyte globulin; Busulfan; Cyclophosphamide; Fludarabine; Mycophenolate mofetil; Sirolimus; Tacrolimus; Thiotepa
- Indications Alpha-thalassaemia; Beta-thalassaemia; Diamond-Blackfan syndrome; Graft-versus-host disease; Sickle cell anaemia
- Focus Therapeutic Use
- 18 Mar 2025 New trial record