A Phase II, Multicentric, Prospective, Non-comparative Clinical Trial to Assess the Efficacy and Safety of the Treatment of Pyruvate Dehydrogenase Deficiency (PDH) Patients With Glycerol Phenybutyrate (RAVICTI)
Latest Information Update: 09 Apr 2025
At a glance
- Drugs Glycerol phenylbutyrate (Primary)
- Indications Pyruvate dehydrogenase complex deficiency disease
- Focus Therapeutic Use
- Acronyms PDH-RAVICTI
- 03 Apr 2025 The protocol has been amended change in time frame.
- 24 Mar 2025 New trial record