An Open-label, Dose-escalation Clinical Trial to Assess the Safety and Efficacy of EXG001-307 After Intrathecal Injection in Patients With Spinal Muscular Atrophy
Latest Information Update: 25 Mar 2025
At a glance
- Drugs EXG001-307 (Primary)
- Indications Spinal muscular atrophy
- Focus Adverse reactions
- Sponsors Hangzhou Jiayin Biotech
- 25 Mar 2025 New trial record