Trial Profile

An Open-label, Multi-center, Phase I/II Study to Assess Safety, Tolerability and Efficacy of DFT383 in Pediatric Participants With Nephropathic Cystinosis

Status: Not yet recruiting

Phase of Trial: Phase I/II

Latest Information Update: 11 Apr 2025

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At a glance

Drugs DFT 383 (Primary) ; Mercaptamine
Indications Nephropathic cystinosis
Focus Adverse reactions; Therapeutic Use
Acronyms CYStem

Most Recent Events

11 Apr 2025 New trial record

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