Trial Profile

A Phase 3 study of rugonersen (RO7248824) in treatment for individuals with Angelman syndrome

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 22 Apr 2025

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At a glance

Drugs Rugonersen (Primary)
Indications Angelman syndrome
Focus Registrational; Therapeutic Use
Sponsors Oak Hill Bio

Most Recent Events

22 Apr 2025 New trial record
16 Apr 2025 According to Oak Hill Bio media release, company plans to initiate this study in early 2026.

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