A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan on Disease Management, Treatment-Related Outcomes and Healthcare Resource Utilization for Adult Patients With Paroxysmal Nocturnal Hemoglobinuria in China
Latest Information Update: 20 Jun 2025
At a glance
- Drugs Iptacopan (Primary) ; Eculizumab
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Therapeutic Use
- Acronyms PNH-NIS
- Sponsors Novartis Pharmaceuticals
Most Recent Events
- 15 Jun 2025 Status changed from not yet recruiting to recruiting.
- 22 Apr 2025 New trial record