Trial Profile

A confirmatory study of TA-ERT for Mucopolysaccharidosis IIIB

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 25 May 2025

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At a glance

Drugs Tralesinidase alfa (Primary)
Indications Mucopolysaccharidosis III
Focus Registrational; Therapeutic Use

Most Recent Events

25 May 2025 New trial record
06 May 2025 According to Spruce Biosciences media release, the company plans to initiate a confirmatory study prior to potential accelerated approval of TA-ERT

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