An Open-label, Single-arm Extension Study to Evaluate the Long-term Safety, Tolerability, and Efficacy of Leniolisib for Immune Dysregulation in Primary Immunodeficiency Disorders
Latest Information Update: 06 Jun 2025
At a glance
- Drugs Leniolisib (Primary)
- Indications Primary immunodeficiency diseases
- Focus Adverse reactions
- Sponsors Pharming Technologies
Most Recent Events
- 30 May 2025 New trial record