A Phase 2a Partially Randomized, Placebo-controlled, Sequential Dose-ranging Study of TTI-0102 in Adults and Children With Leigh Syndrome Spectrum
Latest Information Update: 30 May 2025
At a glance
- Drugs TTI-0102 (Primary) ; Mannitol
- Indications Leigh disease
- Focus Pharmacokinetics
- Sponsors Thiogenesis Therapeutics
Most Recent Events
- 30 May 2025 New trial record