Trial Profile

A phase 3 pivotal,open,single-arm trial of TSHA-102 in patients with Rett syndrome

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 02 Jun 2025

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At a glance

Drugs TSHA 102 (Primary)
Indications Rett syndrome
Focus Registrational; Therapeutic Use

Most Recent Events

02 Jun 2025 New trial record
28 May 2025 According to a Taysha Gene Therapies media release,company plans to submit the pivotal trial protocol and SAP as an amendment to the IND application this quarter and anticipate initiating this pivotal program in the third quarter of 2025.

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