A clinical study of ART001 for the treatment of Transthyretin amyloidosis
Latest Information Update: 06 Jun 2025
At a glance
- Drugs ART-001-AccurEdit-Therapeutics (Primary)
- Indications Transthyretin-related hereditary amyloidosis
- Focus Adverse reactions
Most Recent Events
- 06 Jun 2025 New trial record