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A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1

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Trial Profile

A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1

Status: Not yet recruiting
Phase of Trial: Phase III

Latest Information Update: 14 Jun 2025

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At a glance

  • Drugs Delpacibart etedesiran (Primary)
  • Indications Myotonic dystrophy
  • Focus Adverse reactions
  • Acronyms HARBOR-OLE
  • Sponsors Avidity Biosciences

Most Recent Events

  • 14 Jun 2025 New trial record

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