A Prospective, Non-interventional Study to Evaluate the Efficacy and Safety of Iptacopan in Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH) in Routine Clinical Practice in the Russian Federation
Latest Information Update: 26 Dec 2025
At a glance
- Drugs Iptacopan (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Therapeutic Use
- Acronyms PRIORITY- PNH
- Sponsors Novartis Pharmaceuticals
Most Recent Events
- 07 Aug 2025 Status changed from not yet recruiting to recruiting.
- 02 Jul 2025 New trial record